Older women could be vulnerable to harmful inflammation from new gene therapies to treat incurable eye diseases, new research ...

Researchers have demonstrated, for the first time in the world using mice, the ability to overcome significant challenges in gene therapy using adeno-associated virus vectors (AAV), specifically ...

Gene therapies to treat rheumatoid arthritis have evolved slowly, but one is ready to move into human trials and an ...

A new study reveals that modifying the CUL5 gene enhances CAR-T cell therapy for leukemia and lymphoma. This improves cell ...

The California Institute for Regenerative Medicine has awarded a $6 million grant to USC investigators pioneering a new first ...

The American Cancer Society estimates that 83,000 new cases of bladder cancer will be diagnosed this year, with nearly 17,000 ...

For the last 10 years, the only effective treatment for hypophosphatasia (HPP) has been an enzyme replacement therapy that ...

Five years removed from the COVID-19 outbreak, scientists around the world are still studying its effects and, more importantly, ways those effects can be mitigated in the future.

Adeno-associated virus vectors (AAV vectors), which are used in gene therapy, can introduce genes into various cell types and maintain long-term gene expression, making them clinically applicable ...

The majority are in the very early preclinical stage of development, but applications for regulatory approval have been ...

The University of Southern California (USC) has received a $6m grant from the California Institute for Regenerative Medicine ...