Daily drug can mimic health benefits of high-altitude, low-oxygen living for mitochondrial disease
For the average person, living at high altitude—where oxygen is sparser than at sea level—can have health benefits ranging ...
High-cost sickle cell gene therapies push insurers and Medicaid programs to find new payment models
The high cost of sickle cell gene therapies is pushing private insurers and Medicaid programs to develop new payment models.
Medindia6h
Patented transdermal drug candidate from Vascarta may offer a convenient & cost-effective way to treat sickle cell disease
Vascarta's transdermal curcumin gel formulation ("VAS-101") experienced reduced pain and inflammation along with improved red blood cell stability and functionality. Based in part on these favorable ...
New Vision on MSN11d
Breakthrough sickle cell drug causes excitement
A groundbreaking sickle cell disease treatment has been approved for use in the UK's National Health Service (NHS). The treatment offers patients with severe forms of the condition hope for a ...
EurekAlert!1d
Daily drug captures health benefits of high-altitude, low-oxygen living
Scientists at Gladstone Institutes have developed a drug that mimics the effects of breathing low oxygen. In mice with Leigh Syndrome—the most common childhood mitochondrial disease—the HypoxyStat ...
Health Affairs8d
An Agenda For Sickle Cell Disease Research That Encompasses Lived Experience
As treatment and care continues to evolve, we must ensure that people living with this disease are able to advocate for ...
MedCity News10d
Beyond Drugs: Blood-Based Therapies in Sickle Cell Disease and Beyond
Drug-based therapy, starting with hydroxyurea ... The World Coalition on Sickle Cell Disease, launched in 2023, is an excellent example of the type of collaboration that will be needed to expand ...