More information: Carlo Castruccio Castracani et al, An erythroid-specific lentiviral vector improves anemia and iron metabolism in a new model of XLSA, Blood (2024). DOI: 10.1182/blood.
Patients with XLSA experience a disruption in heme synthesis, leading to a spectrum of issues such as severe anemia and iron overload ... which provide vitamin B6, and blood transfusions to ...