A 3-foot-8 woman with dwarfism gets mistaken for her 5-foot-8 boyfriend’s little sister but says “I don’t care what others say.” Caitlin Hellyer, 23, has achondroplasia dwarfism — a bone ...
The oral FGFR1-3 selective tyrosine kinase inhibitor infigratinib was found to be safe and effective at the highest studied dose among children with achondroplasia in a phase II dose-finding study.
A promising daily tablet is effective at increasing height and improving proportional limb growth in children with achondroplasia, the most common form of dwarfism, according to a new study.