A University of Alberta music professor has turned Edmonton boy Jakob Guziak's rare 'bubble boy disease' into a music using a ...

When Madi Vanstone was 11, she found a medication that would be life changing for her battle against cystic fibrosis, but it ...

CARLSBAD, Calif.-- ( BUSINESS WIRE )--This week, the Association for Creatine Deficiencies ’ (ACD) Vice-Board Chair Jeffrey Randall Allen was crowned champion of Prime Video’s “Beast Games ,” winning ...

It is an especially relevant question for many living with Huntington’s Disease (HD). Notably, some studies have shown that ...

A California resident who was raised in Columbus is $10 million richer after he won "Beast Games" on Amazon Prime.

Making memories is something most people do everyday, sometimes without realizing just how important memories can be.

Total Revenue of $560 million, exceeding guidanceCrysvita® revenue of $410 million and Dojolvi® revenue of $88 million2025 Financial ...

Biomedical engineers at Duke University have demonstrated a promising new approach that could be used to treat a rare and ...

The Rice lab of bioengineer Gang Bao and collaborators at Baylor College of Medicine have developed a new gene-editing strategy that dramatically boosts the effectiveness of gene therapies in the ...